The second child in a healthy family, Tymofii was developing normally in the first days, however, he sadly faced the early onset of SMA already in the third week after birth. The genetic testing soon confirmed the Type 1 diagnosis and tore the parents’ hearts forever apart.

In these 2 years, the family had to learn to build their life into Tymofii’s routines and devices. Tim is taking Risdiplam as a part of Genetec’s Early Access International Program.

The members of the BFS Board of Directors Nataliya Miller and Matt Lambert have been interviewed by KUTV CBS 2 channel

BFS congratulates Dima, his family and the team of volunteers! We are endlessly happy you’ve been given this amazing chance before the age of 2! Hope, the rehabilitation is easy, and the effects of the therapy are going to be stunning. Wishing Dima all the health on the planet!

Sofiia Mykytiuk is 9 months old, she has SMA Type 1. The family decided to immigrate to the US 5 months ago as “Uniting for Ukraine” program participants. After long examinations and tests, Sofiia qualified for Zolgensma therapy and received treatment at Los Angeles Children’s Hospital right after Christmas 2022.

BFS expresses enormous gratitude to all medical professionals and volunteers who made this life-saving journey for Sofiia a reality!